Recent successes and future predictions on drug repurposing for rare diseases

Abstract

Some rare disease treatments come from drug repurposing. The biopharma industry focuses on commercial rare disease drug repurposing, and disease-specific non-profits and governments focus on philanthropic rare disease drug repurposing. In the future, it is likely that both groups will increase their use of drug repurposing as a means of developing treatments for rare diseases, but for different reasons.