The art and science of gene therapy has received much attention of late. The tragic death of 18-year-old Jesse Gelsinger, a volunteer in a Phase I clinical trial, has overshadowed the successful treatment of three children suffering from a rare but fatal immunological disease. In the light of the success and tragedy, it is timely to consider the challenges faced by gene therapy - a novel form of molecular medicine that may be poised to have an important impact on human health in the new millennium.
CITATION STYLE
Somia, N., & Verma, I. M. (2000). Gene therapy: Trials and tribulations. Nature Reviews Genetics. European Association for Cardio-Thoracic Surgery. https://doi.org/10.1038/35038533
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