Lentiviral vectors containing a retinal pigment epithelium specific promoter for leber congenital amaurosis gene therapy: Lentiviral gene therapy for LCA

Bemelmans, A. P., Kostic, C., Hornfeld, D., Jaquet, M., Crippa, S. V., Hauswirth, W. W., … Arsenijevic, Y. (2005). Lentiviral vectors containing a retinal pigment epithelium specific promoter for leber congenital amaurosis gene therapy: Lentiviral gene therapy for LCA. In Advances in Experimental Medicine and Biology (Vol. 572, pp. 247–253).