Muscle‐specific gene editing improves molecular and phenotypic defects in a mouse model of myotonic dystrophy type 1

Mariapaola Izzo; Jonathan Battistini; Elisabetta Golini; Christine Voellenkle; Claudia Provenzano; Tiziana Orsini; Georgios Strimpakos; Ferdinando Scavizzi; Marcello Raspa; Denisa Baci; Svetlana Frolova; Spyros Tastsoglou; Germana Zaccagnini; Jose Manuel Garcia‐Manteiga; Genevieve Gourdon; Silvia Mandillo; Beatrice Cardinali; Fabio Martelli; Germana Falcone

Journal ArticleOPEN ACCESS

Muscle‐specific gene editing improves molecular and phenotypic defects in a mouse model of myotonic dystrophy type 1

Izzo M
Battistini J
Golini E
et al.

Clinical and Translational Medicine (2025) 15(2)

DOI: 10.1002/ctm2.70227

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Abstract

Graphical Abstract Clin. Transl. Med. 2025;15:e70227. wileyonlinelibrary.com/journal/ctm2 https://doi.

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APA

Izzo, M., Battistini, J., Golini, E., Voellenkle, C., Provenzano, C., Orsini, T., … Falcone, G. (2025). Muscle‐specific gene editing improves molecular and phenotypic defects in a mouse model of myotonic dystrophy type 1. Clinical and Translational Medicine, 15(2). https://doi.org/10.1002/ctm2.70227

Muscle‐specific gene editing improves molecular and phenotypic defects in a mouse model of myotonic dystrophy type 1

Abstract

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