Abstract
CEP290-associated inherited retinal degeneration causes severe early-onset vision loss due to pathogenic variants in CEP290. EDIT-101 is a clustered regularly interspaced short palindromic repeats ...
Cite
CITATION STYLE
APA
Pierce, E. A., Aleman, T. S., Jayasundera, K. T., Ashimatey, B. S., Kim, K., Rashid, A., … Pennesi, M. E. (2024). Gene Editing for CEP290 -Associated Retinal Degeneration. New England Journal of Medicine, 390(21), 1972–1984. https://doi.org/10.1056/nejmoa2309915
Register to see more suggestions
Mendeley helps you to discover research relevant for your work.
Already have an account? Sign in
Sign up for free