American Society of Gene Therapy - Tenth annual meeting

Abstract

At present, gene transfer technology is a useful tool for the engineering of animal and cell-culture models for the study of various pathological conditions. Achieving more effective human gene therapy clinical trials requires improvements in vector design, both in terms of safety and transduction efficiency, particularly for the in vivo modality of gene transfer. Encouraging progress is reported in the field of gene therapy every year; however, the successful application of gene therapy programs in the clinical setting still requires enormous further research effort. © The Thomson Corporation.